Pablo Perez-Pinera

Pablo Perez-Pinera
Pablo Perez-Pinera
  • Associate Professor
3252 Everitt Laboratory

Primary Research Area

  • Synthetic Bioengineering

Research Areas

  • Biomolecular engineering
  • Gene and cell therapy
  • Genome engineering
  • Regenerative medicine
  • Regenerative tissue engineering

For More Information

Service to Federal and State Government

  • TAG study section member

Research Interests

  • Neuromuscular diseases
  • Neurodegenerative diseases
  • Biopharmaceutical Production
  • Gene Therapy
  • Regenerative Medicine
  • Genome Engineering
  • Synthetic Biology

Primary Research Area

  • Synthetic Bioengineering

Research Areas

  • Biomolecular engineering
  • Gene and cell therapy
  • Genome engineering
  • Regenerative medicine
  • Regenerative tissue engineering

Selected Articles in Journals

Pending Articles

  • 1. Miskalis A, Shirguppe S, Winter J, Elias G, Swami D, Nambiar A, Stilger M, Woods W, Gosstola N, Gapinske M, Zeballos A, Moore H, Maslov S, Gaj T and Perez-Pinera P. SPLICER: A Highly Efficient Base Editing Toolbox That Enables In Vivo Therapeutic Exon Skipping. Under review Nat Commun.